Clinical Trials

A Study Evaluating the Safety and Efficacy of EDIT-301 in Participants With Severe Sickle Cell Disease (RUBY)

Addition of JSP191 (C-kit Antibody) to Nonmyeloablative Hematopoietic Cell Transplantation for Sickle Cell Disease and Beta-Thalassemia

Haploidentical Transplantation With Pre-Transplant Immunosuppressive Therapy for Patients With Sickle Cell Disease

Identifying Barriers and Strategies to Support Self-efficacy for Medication Adherence With Text Messaging

Prevention of Malnutrition in Children With Sickle Cell Disease

TMLI and Alemtuzumab for Treatment of Sickle Cell Disease

MAP to Provide Access to Crizanlizumab, for Sickle Cell Disease Patients

A GBT021601 ADME Microtracer Study in Healthy Volunteers

A Study Evaluating the Safety and Efficacy of LentiGlobin BB305 Drug Product in β-Thalassemia Major (Also Referred to as Transfusion-dependent β-Thalassemia [TDT]) and Sickle Cell Disease

A Study to Assess the Safety, Tolerability, and Efficacy of BIVV003 for Autologous Hematopoietic Stem Cell Transplantation in Patients With Severe Sickle Cell Disease

Abatacept for GVHD Prophylaxis After Hematopoietic Stem Cell Transplantation for Pediatric Sickle Cell Disease

Decision Aid for Therapeutic Options In Sickle Cell Disease

Hydroxyurea and Erythropoietin to Treat Sickle Cell Anemia

Improving Parental Psychosocial Functioning and Early Developmental Outcomes in Children With Sickle Cell Disease

Improving Self-Management in Adolescents With Sickle Cell Disease

Iron Overload Assesment in Sickle Cell Anemia and Sickle Cell Thalassemia

L-Glutamine Therapy for Sickle Cell Anemia and Sickle ß0 Thalassemia

Laboratory-based Hypnosis Intervention on Pain Responsivity in Adolescents With Sickle Cell Disease

Losartan for Sickle Cell Kidney Disease

Mobilization and Handling of Stem Cells for Transplant From Healthy Volunteers With Sickle Cell Trait