Clinical Trials

Allogeneic Hematopoietic Stem Cell Transplant for Patients With Primary Immune Deficiencies

Conditioning SCID Infants Diagnosed Early

Immune Disorder HSCT Protocol

Expanded Access to CD34+ Selection Utilizing Miltenyi CliniMACS Prodigy® for Patients Receiving Peripheral Blood Stem Cell Transplantations and Stem Cell Boosts

Baby Detect : Genomic Newborn Screening

Developing Newborn Screening for Infants With Primary Immunodeficiency

Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID

EZN-2279 in Patients With ADA-SCID

Fludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem Cell Transplant in Treating Patients With Hematologic Malignancies

Gene Therapy for X-linked Severe Combined Immunodeficiency

Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral Vector

Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency

Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study

Generalized Neonatal Screening of Severe Combined Immunodeficiencies

IMM 0212: Busulfan With Fludarabine and Antithymocyte Globulin as Preparative Therapy for Hematopoietic Stem Cell Transplant for the Treatment of Severe Congenital T-Cell Immunodeficiency

MND-ADA Transduction of CD34+ Cells From Children With ADA-SCID

Newborn Screening for Severe Combined Immunodeficiency (SCID) in a High-Risk Population

Rapid Infusion of Immune Globulin Intravenous (Human) In Primary Immunodeficiency Patients

Study Through Imaging of Visceral Lymphoid Organs in Patients With SCID Who Have Recieved Bone Marrow Allograft

The Role of Bacteria and Genetic Variations in Cystic Fibrosis