Clinical Trials

50 trials registered for Severe combined immunodeficiency (SCID) / combined immunodeficiency syndromes

A Single-arm Safety Study of Transplantation Using Umbilical Cord Blood and Human Placental-derived Stem Cells From Partially Matched Related Donors in Persons With Certain Malignant Blood Diseases and Non-malignant Disorders
NCT00596999N/ACelgene Corporation
Unknown
Clinical Characteristics and Genetic Profiles of Severe Combined Immunodeficiency in China
NCT02231983N/AShanghai Children's Medical Center
Unknown
Evaluation of Adenosine Deaminase (ADA) Enzyme Deficiency in Patients With Lymphopenia and/or Elevated Immunoglobulin E
NCT05300373N/ATRPHARM
Unknown
Gene Therapy for X Linked Severe Combined Immunodeficiency
NCT04286815N/AChildren's Hospital of Chongqing Medical University
Unknown
Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1)
NCT01175239N/AGreat Ormond Street Hospital for Children NHS Foundation Trust
Unknown
Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy
NCT04959890N/AFondazione Telethon
Unknown
Observational Study Evaluating the Prevalence of Enzyme Deficiency in Pulmonology Clinics (ADA)
NCT05300347N/ATRPHARM
Unknown
Patients Treated for SCID (1968-Present)
NCT01346150N/ANational Institute of Allergy and Infectious Diseases (NIAID)
Unknown
Safety and Early Efficacy Study of TBX-1400 in Patients With Severe Combined Immunodeficiency
NCT02860559Phase 1Taiga Biotechnologies, Inc.
Unknown
Sirolimus Prophylaxis for aGVHD in TME SCID
NCT02177760Phase 2University of California, San Francisco
Withdrawn