Clinical Trials
10 trials registered for Aromatic L-amino acid decarboxylase deficiency
A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Participants
NCT04903288Phase 2PTC Therapeutics
Active↗
A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion
NCT02926066Phase 2National Taiwan University Hospital
Completed↗
A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC
NCT01395641Phase 1/2National Taiwan University Hospital
Completed↗
Baby Detect : Genomic Newborn Screening
NCT05687474N/ACentre Hospitalier Universitaire de Liege
Completed↗
Genetic Etiology in Patients With Cerebral Palsy
NCT05123768N/AUniversity Medical Centre Ljubljana
Completed↗
Newborn Screening for Aromatic L-amino Acid Decarboxylase Deficiency
NCT02399761N/ANational Taiwan University Hospital
Completed↗
A Trial to Evaluate Safety and Efficacy of a Product Named VGN-R09b in Severe AADC Deficiency
NCT06432140Phase 1Shanghai Vitalgen BioPharma Co., Ltd.
Not Yet Recruiting↗
A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients
NCT02852213Phase 1Krzysztof Bankiewicz
Recruiting↗
An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.
NCT05765981Early Phase 1Shanghai Jiao Tong University School of Medicine
Recruiting↗
Prevalence of High Plasmatic 3OMethyldopa Level in a Specific Population of Patients With a Symptomatology Compatible With AADC Deficiency
NCT05211609N/AUniversity Hospital, Montpellier
Unknown↗