Clinical Trials

Studies in Patients With Tuberous Sclerosis Complex

Study of ANAVEX2-73 in Patients With Rett Syndrome

The Role of Dietary Calcium for the Treatment of Osteopenia in Girls With Rett Syndrome

To Study the Efficacy & Safety of Oral NA-921 (Bionetide) in Girls and Women with Rett Syndrome

Tolerability of the Immersive Virtual Reality System Grail in Subjects Affected by Rett Syndrome

Parent and Infant Inter(X)Action Intervention (PIXI)

Efficacy and Safety of NTI164 in Children and Young Adults With Rett Syndrome

A Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study)

Cognitive Function in Rett Syndrome During Trofinetide Treatment

GROWing Up With Rare GENEtic Syndromes

Intensive Multimodal Neurorehabilitation Targeting Neuroplasticity in Pediatric Neurodevelopmental and Chromosomal Disorders

Measuring Impact of Computer Gaming on Arm Use in Rett Syndrome

Neurophysiologic Biomarkers in Rett Syndrome

Repurposing Mirtazapine in Rett Syndrome

Rett Syndrome Registry

The Rett Syndrome Global Registry

To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome

Validating Innovative Biosensors for Rett Autonomic Symptom Tracking

Web Intervention for Parents of Youth With Genetic Syndromes (WINGS)

A Long-term Safety Study of Cannabidiol Oral Solution (GWP42003-P, CBD-OS) in Patients With Rett Syndrome