Clinical Trials

Cerliponase Alfa Observational Study in the US

Gene Therapy for Children With CLN3 Batten Disease

Natural History of Neuronal Ceroid Lipofuscinosis, Batten's CLN6 Diseae

Study for the Treatment for CLN7 Disease

An Open-label Safety, Pharmacokinetic, and Efficacy Study of Miglustat for the Treatment of Subjects With Batten Ceroid Lipofuscinosis, Neuronal 3 (CLN3) Disease

Cellcept for Treatment of Juvenile Neuronal Ceroid Lipofuscinosis

Functional Near-Infrared Spectroscopy (fNIRS) Combined With Diffuse Correlation Spectroscopy (DCS) in Neurocognitive Disease as Compared to Healthy Neurotypical Controls

Neuronal Ceroid Lipofuscinosis and Associated Sleep Abnormalities

Trehalose in Subjects With Neuronal Ceroid Lipofuscinoses

Safety, Tolerability, and Efficacy of PLX-200 in Patients With CLN3

Caregiving Networks Across Disease Context and the Life Course

Clinical and Neuropsychological Investigations in Batten Disease

Inherited Retinal Degenerative Disease Registry

Investigations of Juvenile Neuronal Ceroid Lipofuscinosis

Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD Database

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

Natural History Study of Batten Disease

Optic-to-Audio Device in a Pediatric Cohort With CLN3-related Conditions or Low Vision

Using NPT to Evaluate Providing PPC as ELNEC-PPC WBT for Nurses

Safety and Efficacy Study of HuCNS-SC in Subjects With Neuronal Ceroid Lipofuscinosis