Clinical Trials

6 trials registered for PLA2G6-associated neurodegeneration (PLAN) / Neurodegeneration with brain iron accumulation 2A (NBIA2A)

A Study to Assess Efficacy and Safety of RT001 in Subjects With Infantile Neuroaxonal Dystrophy

NCT03570931Phase 2/3Biojiva LLC

Active↗

A Natural History Study of Infantile Neuroaxonal Dystrophy

NCT04027816N/ABiojiva LLC

Completed↗

Natural History of Infantile Neuroaxonal Dystrophy

NCT03999814N/ABiojiva LLC

Completed↗

TIRCON International NBIA Registry

NCT05522374N/ALMU Klinikum

Recruiting↗

Desipramine in Infantile Neuroaxonal Dystrophy (INAD).

NCT03726996Phase 4Duke University

Terminated↗

NBIAready: Online Collection of Natural History Patient-reported Outcome Measures

NCT02587858N/ASusan J. Hayflick

Unknown↗