Clinical Trials

30 trials registered for Adenosine deaminase-deficient severe combined immunodeficiency

Gene Therapy for ADA-SCID Using an Improved Lentiviral Vector (Ivlv-ADA)

NCT03645460N/AShenzhen Geno-Immune Medical Institute

Recruiting↗

Gene Therapy for Adenosine Deaminase Severe Combined Immune Deficiency Using Peripheral Blood and EFS ADA Vector

NCT05432310Phase 1/2University of California, Los Angeles

Recruiting↗

Evaluation of Adenosine Deaminase (ADA) Enzyme Deficiency in Patients With Lymphopenia and/or Elevated Immunoglobulin E

NCT05300373N/ATRPHARM

Unknown↗

Investigation of ADA Enzyme Deficiency

NCT05300334N/ATRPHARM

Unknown↗

Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy

NCT04959890N/AFondazione Telethon

Unknown↗

Observational Study Evaluating the Prevalence of Enzyme Deficiency in Pulmonology Clinics (ADA)

NCT05300347N/ATRPHARM

Unknown↗

Patients Treated for SCID (1968-Present)

NCT01346150N/ANational Institute of Allergy and Infectious Diseases (NIAID)

Unknown↗

A Clinical Study to Enable Process Validation of Commercial Grade OTL-101

NCT04140539Phase 2/3University of California, Los Angeles

Withdrawn↗

Quality of Life and Neuropsychiatric Sequelae in Patients Treated With Gene Therapy for ADA-SCID and in Their Parents

NCT01182857N/ANational Human Genome Research Institute (NHGRI)

Withdrawn↗

Retroviral Insertion Site Methodology Study

NCT03311074Phase 4Fondazione Telethon

Withdrawn↗