Clinical Trials

Efficacy and Safety of SYNB1934 in Patients With PKU (SYNPHENY-3)

Long-Term Tetrahydrobiopterin Treatment in PKU Patients of 0-18 Years - Study on Phenylalanine Tolerance and Safety

Moderate Intensity Exercise and Phenylketonuria

Safety and Efficacy of HMI-103 in Participants With Classical PKU Due to PAH Deficiency

Sapropterin on Cognitive Abilities in Young Adults With Phenylketonuria

A Study Into the Future Cardiovascular Disease (CVD) Risk of Phenylketonuria (PKU) Patients on a Low Phenylalanine Treatment Diet (LPD).

Evaluation of Capillary Blood Collection Devices (Mitra® and HemaPEN®)

A Dose-finding Study to Evaluate mRNA-3210 in Participants With Phenylketonuria

PKU Low Calorie Drink Study

Safety, Tolerability, Pharmacodynamics and Pharmacokinetics of CDX 6114 in PKU Patients